News

aTyr’s Immunomodulatory Therapy ATYR1923 Wins Orphan Drug Status

The U.S. Food and Drug Administration has granted orphan drug designation to aTyr Pharma’s experimental immunomodulatory molecule ATYR1923 for the treatment of sarcoidosis. The therapy is being developed for severe inflammatory diseases affecting the lungs, which in sarcoidosis patients is called pulmonary sarcoidosis. Orphan drug status is given to…

INOpulse Shows Promise in Proof-of-concept Trial for PH-Sarcoidosis

INOpulse, a device that administers inhaled nitric oxide, significantly improved blood flow parameters in a small proof-of-concept clinical trial conducted in people with pulmonary hypertension associated with sarcoidosis (PH-Sarc). “We are pleased with the positive top-line data from this proof-of-concept study,” Naseem Amin, MD, chairman of the board…

FSR Small Research Grants Aim to Improve Patient Outcomes

Two university professors have each been awarded $25,000 small research grants from the Foundation for Sarcoidosis Research (FSR) to pursue projects aimed at improving outcomes for people with sarcoidosis. Researcher Maneesh Bhargava, MD, PhD, of the University of Minnesota, will use the grant to focus on inflammation in…

U.S. Researchers Invited to Apply for Ann Theodore Foundation Grants

A new grant program worth up to $3.5 million, from the Ann Theodore Foundation, is seeking researchers in the U.S. who are working to advance knowledge and understanding of sarcoidosis. The Milken Institute, a nonprofit think tank, is accepting applications from American research institutions for the Ann Theodore…

RARE-X, Global Genes to Help Collect Rare Disease Patient Data

In their continued efforts to improve health equity for people with rare diseases, Global Genes and RARE-X have joined forces to help advocacy groups collect patient data and make the most of that information. “Patient data is perhaps the most valuable asset rare disease communities can leverage to…